I'm specifically interested in SDS, which is a rare genetic disease that impacts blood production. It seems like numerous viable options exist for the modification of hematopoietic stem cell DNA, which I believe would partially cure the disease. Is this not just a matter of extraction (marrow) -> isolation -> modification -> confirmation -> implantation? What is holding us back?<p>Some references:
* DIY genetic engineering kit:
http://www.the-odin.com/genetic-engineering-home-lab-kit/<p>* Order custom CRISPR lentivirus vectors here:
https://crispr.sigmainformatics.com/templates/CRISPR%20Custom%20Editable%20PDF_v8_savable.pdf